172
Participants
Start Date
January 1, 2023
Primary Completion Date
January 31, 2040
Study Completion Date
January 31, 2040
Hemophilia Center of Western Pennsylvania, Pittsburgh
UCN Hemophilia and Thrombosis Center, Shandon
St Joseph's Children's Hospital, Center for Bleeding and Clotting Disorders, Tampa
Hemophilia and Thrombosis Center at the University of Colorado Anschutz Medical Campus, Aurora
Orthopedic Institute for Children, Orthopedic Hemophilia Treatment Center, Los Angeles
UC Davis Hemophilia Treatment Center, Sacramento
University of Michigan, Pediatric Hematology and Oncology, Ann Arbor
Addenbrooke's Hospital, Hemophilia and Thrombophilia Center, Cambridge
Hammersmith Hospital, Clinical Research Facility, Centre for Translational and Experimental Medicine, London
Queen Elizabeth Hospital Birmingham. Adult Hemophilia Centre, West Midlands Adult Comprehensive Care Hemophilia Centre, London
Royal London Hospital, Barts and the London Hemophilia Center, London
St Thomas' Hospital, Centre for Hemophilia, Hemostasis and Thrombosis, London
University Hospital Southampton NHS Foundation Trust, Southampton
Lead Sponsor
BioMarin Pharmaceutical
INDUSTRY