A Long-Term Follow-Up Study in Severe Hemophilia A Subjects Who Received BMN 270 in a Prior BioMarin Clinical Trial (270-401)

Enrolling by invitationOBSERVATIONAL
Enrollment

172

Participants

Timeline

Start Date

January 1, 2023

Primary Completion Date

January 31, 2040

Study Completion Date

January 31, 2040

Conditions
Hemophilia A
Trial Locations (13)

15213

Hemophilia Center of Western Pennsylvania, Pittsburgh

27517

UCN Hemophilia and Thrombosis Center, Shandon

33614

St Joseph's Children's Hospital, Center for Bleeding and Clotting Disorders, Tampa

80045

Hemophilia and Thrombosis Center at the University of Colorado Anschutz Medical Campus, Aurora

90007

Orthopedic Institute for Children, Orthopedic Hemophilia Treatment Center, Los Angeles

95817

UC Davis Hemophilia Treatment Center, Sacramento

48109-5718

University of Michigan, Pediatric Hematology and Oncology, Ann Arbor

Unknown

Addenbrooke's Hospital, Hemophilia and Thrombophilia Center, Cambridge

Hammersmith Hospital, Clinical Research Facility, Centre for Translational and Experimental Medicine, London

Queen Elizabeth Hospital Birmingham. Adult Hemophilia Centre, West Midlands Adult Comprehensive Care Hemophilia Centre, London

Royal London Hospital, Barts and the London Hemophilia Center, London

St Thomas' Hospital, Centre for Hemophilia, Hemostasis and Thrombosis, London

University Hospital Southampton NHS Foundation Trust, Southampton

Sponsors
All Listed Sponsors
lead

BioMarin Pharmaceutical

INDUSTRY