Ruxolitinib as First Line Treatment in Primary Haemophagocytic Lymphohistiocytosis (R-HLH)

PHASE2Not yet recruitingINTERVENTIONAL
Enrollment

20

Participants

Timeline

Start Date

March 31, 2024

Primary Completion Date

November 30, 2026

Study Completion Date

November 30, 2027

Conditions
Haemophagocytic Lymphohistiocytosis
Interventions
DRUG

Ruxolitinib

"Form: tablets, 50 mg/m2/day in two administrations. Maximum dose is 100 mg/day. Administration in association with Methylprednisolone IV (or Prednisolone PO) starting at 2 mg/kg/day in two administrations.~Duration of treatment: until D-1 of conditioning for allogeneic HSCT OR 9weeks for patients who are not eligible for HSCT."

All Listed Sponsors
lead

Assistance Publique - Hôpitaux de Paris

OTHER