Long-term Safety of BCX9930 in Participants With Paroxysmal Nocturnal Hemoglobinuria

PHASE2TerminatedINTERVENTIONAL
Enrollment

28

Participants

Timeline

Start Date

January 18, 2023

Primary Completion Date

January 31, 2025

Study Completion Date

January 31, 2025

Conditions
Paroxysmal Nocturnal Hemoglobinuria
Interventions
DRUG

BCX9930

Taken orally at 400 mg twice daily (BID)

Trial Locations (11)

Unknown

Investigative Site, Paris

Investigative Site, Budapest

Investigative Site, Ampang

Investigative Site, Bloemfontein

Investigative Site, Cape Town

Investigative Site, Pretoria

Investigative Site, Daejeon

Investigative Site, Barcelona

Investigative Site, Valencia

Investigative Site, Leeds

Investigative Site, London

Sponsors
All Listed Sponsors
lead

BioCryst Pharmaceuticals

INDUSTRY