A Longitudinal, Observational Study of Primary Ciliary Dyskinesia in Adults

Active, not recruitingOBSERVATIONAL
Enrollment

50

Participants

Timeline

Start Date

March 8, 2023

Primary Completion Date

April 28, 2025

Study Completion Date

June 30, 2025

Conditions
Primary Ciliary Dyskinesia
Interventions
DIAGNOSTIC_TEST

Spirometry

To assess lung function

DIAGNOSTIC_TEST

Multiple Breath Washout (MBW)

To measure Lung Clearance Index (LCI)

DIAGNOSTIC_TEST

Mucociliary Clearance (MCC)

To measure lung clearance after the inhalation of radiolabeled particles

DIAGNOSTIC_TEST

CT of the chest

Low radiation to assess structural lung disease

DIAGNOSTIC_TEST

MRI of the chest

To assess lung function and structural lung disease

Trial Locations (1)

27599

University of North Carolina at Chapel Hill, Chapel Hill

Sponsors
All Listed Sponsors
collaborator

University of North Carolina, Chapel Hill

OTHER

lead

ReCode Therapeutics

INDUSTRY

NCT05685186 - A Longitudinal, Observational Study of Primary Ciliary Dyskinesia in Adults | Biotech Hunter | Biotech Hunter