48
Participants
Start Date
July 27, 2023
Primary Completion Date
December 4, 2025
Study Completion Date
December 4, 2025
Alogabat
Alogabat will be administered QD with dose depending on cohort and age of the participant.
Queensland Children?s Hospital, South Brisbane
Columbia University Medical Center, New York
Hopital la Timone Enfants, Marseille
IRCCS Istituto G. Gaslini, Genoa
CHU Dijon Bourgogne Hôpital François Mitterand, Dijon
Carolina Institute for Development DisabilitiesUniversity of North Carolina/School of Medicine, Carrboro
Hospital Universitario Puerta De Hierro Majadahonda, Madrid
CHRU de Brest, Brest
Hospital Universitario de Navarra;Unidad de Neuropediatría, Pamploa
IRCCS Eugenio Medea, Conegliano Veneto (TV)
Rush Medical Center, Chicago
Groupe Hospitalier Necker Enfants Malades, Paris
Dr. Von Haunersches Kinderspital, München
Rady Children's Hospital - San Diego, San Diego
Multicare Institute for Research and Innovation, Tacoma
Boston Children's Hospital, Boston
Vanderbilt Children's Hospital, Nashville
Ospedale Pediatrico Bambino Gesù, Rome
Hospital Sant Joan de Deu, Esplugues de Llobregat · Barcelona
Corporacio Sanitaria Parc Tauli, Sabadell
Hoffmann-La Roche
INDUSTRY