16
Participants
Start Date
March 15, 2023
Primary Completion Date
December 31, 2025
Study Completion Date
December 31, 2026
TPN-101
100 mg/ day up to 400mg/day of TPN-101
SST Fatebenefratelli Sacco, Milan
Presidio Ospedale dei Bambini [Children's Hospital], Brescia
Istituto Neurologico Casimiro Mondino, Pavia
Laboratory of Neurogenetics and Neuroinflammation Imagine Institute - INSERM U1163, Paris
Royal Hospital for Children and Young People, Edinburgh
Transposon Therapeutics, Inc.
INDUSTRY