Open-label Study of Adjunctive GNX Treatment in Children and Adults With TSC-related Epilepsy

PHASE3TerminatedINTERVENTIONAL
Enrollment

117

Participants

Timeline

Start Date

May 16, 2022

Primary Completion Date

April 2, 2025

Study Completion Date

April 2, 2025

Conditions
Tuberous Sclerosis Complex
Interventions
DRUG

Ganaxolone

GNX will be administered.

Trial Locations (54)

1454

Epilepsiezentrum Kleinwachau gGmbH, Radeberg

8025

Hospital de la Santa Creu i Sant Pau, Barcelona

8950

Hospital Sant Joan de Déu, Barcelona

14642

University of Rochester Medical Center, Rochester

16147

Pediatric Neurology and Muscular Diseases Unit - University of Genoa, Genova

19803

Nemours Children's Hospital - Delaware Valley, Wilmington

27599

University of North Carolina at Chapel Hill, Chapel Hill

27712

Duke University Medical Center, Durham

28009

Hospital Infantil Universitario Niño Jesús, Madrid

28034

Hospital Ruber International, Madrid

28207

Atrium Health/Levine Children's Hospital, Charlotte

29010

Hospital Regional Universitario de Málaga, Málaga

33617

Epilepsie-Zentrum Bethel - Krankenhaus Mara, Bielefeld

35000

Hôpital Sud, Rennes

38103

Le Bonheur Children's Hospital, Memphis

45229

Cincinnati Children's Hospital Medical Center, Cincinnati

46026

Hospital Universitario y Politécnico La Fe, Valencia

53127

University Hospital Bonn, Bonn

55905

Mayo Clinic - Rochester, Rochester

58313

Gemeinschaftskrankenhaus Herdecke, Herdecke

60528

ZNN - Epilepsiezentrum Frankfurt am Main, Frankfurt

64108

Children's Mercy Hospital, Kansas City

67084

University of Strasbourg, Strasbourg

69229

University Hospital of Lyon, Bron

72202

Arkansas Children's Research Institute, Little Rock

75207

University of Texas Southwestern Medical Center, Dallas

77030

McGovern Medical School at the University of Texas Health Science Center, Houston

78757

Child Neurology Consultants of Austin (CNCA), Austin

79106

Universitäts Krankenhaus Freiburg, Freiburg im Breisgau

80045

Children's Hospital Colorado, Aurora

84108

University of Utah Health Care-Pediatric Neurology, Salt Lake City

90095

UCLA Mattel Children's Hospital, TSC Center, Los Angeles

92123

Rady Children's Hospital - San Diego, San Diego

92868

Children's Hospital of Orange County, Orange

98105

Seattle Children's Hospital, Seattle

100034

Peking University First Hospital, Beijing

100045

Beijing Children Hospital, Capital Medical University, Beijing

100853

Chinese PLA General Hospital, Beijing

130021

First Hospital of Jilin University, Jilin

550004

The Affiliated Hospital of Guizhou Medical University, Beijing

4920235

Schneider Children´s Medical Center, Petah Tikva

02115

Boston Children's Hospital, Harvard Medical School, Boston

VIC 3084

Austin Health, Heidelberg

QLD 4029

Royal Brisbane and Women's Hospital, Herston

VIC 3004

Alfred Health, Melbourne

VIC 3050

Royal Melbourne Hospital, Parkville

H2X 0C2

Hôtel Dieu de Montréal - CHUM, Montreal

H3T 1C5

CHU Sainte-Justine, Montreal

M5G 1X8

The Hospital for Sick Children, Toronto

M5T 2S8

Toronto Western Hospital, Toronto

V6H 3V4

BC Children's Hospital, Vancouver

00185

Policlinico Umberto I, Rome

BS2 8AE

Bristol Royal Hospital for Children, Bristol

S10 2TH

Sheffield Children's Hospital, Sheffield

Sponsors
All Listed Sponsors
lead

Marinus Pharmaceuticals

INDUSTRY

NCT05604170 - Open-label Study of Adjunctive GNX Treatment in Children and Adults With TSC-related Epilepsy | Biotech Hunter | Biotech Hunter