Natural History of Danon Disease

CompletedOBSERVATIONAL
Enrollment

59

Participants

Timeline

Start Date

September 26, 2022

Primary Completion Date

October 31, 2023

Study Completion Date

October 31, 2023

Conditions
Danon Disease
Interventions
PROCEDURE

Heart Transplant

Patients who have undergone a heart transplant as standard of care (SOC) procedure

DEVICE

Cardiac Assistive Device

Patients who have undergone a placement of a cardiac assistive device

Trial Locations (15)

14021

Institut klinické a experimentální medicíny (IKEM)- Institute for Clinical and Experimental Medicine, Prague

24127

Ospedale Papa Giovanni XXIII di Bergamo ASST Pap Giovanni XXIII Hospital, Bergamo

28046

Hospital Universitario La Paz - La Paz University Hospital, Madrid

28222

Hospital Universitario Puerta de Hierro Majadahonda Puerta de Hierro Majadahonda - University Hospital, Madrid

29010

Hospital Universitario Virgen de la Victoria- Virgen de la Victoria University Hosptial, Málaga

34137

IRCCS Burlo Garogolo- Hospital Burlo Garofolo, Trieste

35033

CHU de Rennes, Hôpital Pontchaïllou, Rennes

44800

CHU de Nantes, Hôpital Laennec, Nantes

46026

Hospital Universitario y Politécnico La Fe, Instituto De Investigación Sanitaria La Fe, La Fe University and Polytechnic Hospital, Valencia

50134

University of Florence Dept. of Experimental and Clinical Medicine, Florence

75013

APHP, Hôpital de la Pitié Salppêtrière - Charles Foix, Paris

326312

Hospital Álvaro Cunqueiro, Pontevedra

D07 R2WY

Mater Misericordiae University Hospital, Dublin

08907

Hospital Clínic de Barcelona - Barnaclínic+, Barcelona

Hospital Universitario de Bellvitge- Bellvitge University Hospital, Barcelona

All Listed Sponsors
lead

Rocket Pharmaceuticals Inc.

INDUSTRY