76
Participants
Start Date
October 24, 2022
Primary Completion Date
February 28, 2026
Study Completion Date
February 28, 2026
Sevasemten Dose 1
Sevasemten is administered orally once per day
Sevasemten Dose 2
Sevasemten is administered orally once per day
Sevasemten Dose 3
Sevasemten is administered orally once per day
Sevasemten Dose 4
Sevasemten is administered orally once per day
Sevasemten Dose 5
Sevasemten is administered orally once per day
Placebo
Placebo is administered orally once per day
Kennedy Krieger Institute, Baltimore
Rare Disease Research, Atlanta
University of Florida, Gainesville
Nationwide Children's Hospital, Columbus
Cincinnati Children's Hospital, Cincinnati
University of Iowa, Iowa City
Washington University School of Medicine, St Louis
University of Kansas Medical Center, Kansas City
Arkansas Children's Hospital, Little Rock
Cook Children's Medical Center, Fort Worth
Children's Hospital Colorado, Aurora
UCLA Medical Center, Los Angeles
UC Davis Medical Center, Sacramento
University of Massachusetts Memorial Medical Center, Worcester
Lead Sponsor
Edgewise Therapeutics, Inc.
INDUSTRY