Oral N-acetylcysteine for Retinitis Pigmentosa

PHASE3Active, not recruitingINTERVENTIONAL
Enrollment

483

Participants

Timeline

Start Date

October 11, 2023

Primary Completion Date

May 31, 2029

Study Completion Date

May 31, 2029

Conditions
Retinitis Pigmentosa
Interventions
DRUG

N-acetylcysteine

After randomization, participants will be given about 10-months supply of study drug (intervention), with instructions to take 3 effervescent tablets in water twice a day. They will return to the clinic at M4.5 for evaluation and then at M9, M18, M27, M36, M40.5 and M45. At each in-clinic visit, drug reconciliation will occur. At each visit at Baseline, M9, M18, M27, M36, that is, every 9 months, participants will be given another 10-month supply of study drug.

DRUG

Placebo

After randomization, participants will be given about 10-months supply of placebo, with instructions to take 3 effervescent tablets in water twice a day. They will return to the clinic at M4.5 for evaluation and then at M9, M18, M27, M36, M40.5 and M45. At each in-clinic visit, efficacy and safety assessments will be done and drug reconciliation will occur. At baseline, M9, M18, M27, and M36 participants will be given another 10-month supply of placebo.

Trial Locations (31)

8036

Medical University of Graz, Department of Ophthalmology, Graz

19104

Scheie Eye Institute, Philadelphia

21287

Wilmer Eye Institute- Johns Hopkins University, Baltimore

30322

Emory University, Emory Eye Center, Atlanta

32209

University of Florida - Jacksonville, UF Health Jacksonville, Jacksonville

32607

Vitreo Retinal Associates, Gainesville

33136

University of Miami, Bascom Palmer Eye Institute, Miami

37211

Vanderbilt University, Vanderbilt Eye Institute, Nashville

48105

University of Michigan, Kellogg Eye Center, Ann Arbor

52242

University of Iowa, Carver College of Medicine, Iowa City

53226

Medical College of Wisconsin, The Eye Institute, Milwaukee

53705

University of Wisconsin - Madison, McPherson Eye Research Institute, Madison

55455

University of Minnesota, Department of Ophthalmology and Visual Neurosciences, Minneapolis

55905

Mayo Clinic, Department of Ophthalmology, Rochester

60208

Northwestern University, Evanston

60612

University Of Illinois At Chicago, Chicago

72076

University of Tübingen, Department für Augenheilkunde, Tübingen

73104

University of Oklahoma, Dean McGee Eye Institute, Oklahoma City

75231

Retina Foundation of the Southwest, Dallas

84132

University of Utah, Moran Eye Center, Salt Lake City

90089

University of Southern California, Keck School of Medicine, Los Angeles

94158

University of California - San Francisco, Department of Ophthalmology, San Francisco

94303

Stanford University, Byers Eye Institute, Stanford

95817

University of California - Davis, Department of Ophthalmology & Vision Science, Davis

98109

University of Washington, Department of Ophthalmology, Seattle

02114

Harvard University, Mass. Eye and Ear, Boston

H4A 3J1

McGill University, The Research Institute of the McGill University Health Center, Montreal

6500 HB

Radboud University, Radboud University Medical Centre, Nijmegen

1105 AZ

University of Amsterdam, Amsterdam Medical Center, Amsterdam

CH-4031

Universitätsspital Basel, Eye Clinic, Basel

Unknown

University College London, Moorfields Eye Hospital, London

Sponsors
All Listed Sponsors
collaborator

National Eye Institute (NEI)

NIH

collaborator

Duke University

OTHER

collaborator

Emory University

OTHER

collaborator

Massachusetts Eye and Ear Infirmary

OTHER

collaborator

Mayo Clinic

OTHER

collaborator

Medical College of Wisconsin

OTHER

collaborator

Retina Foundation of the Southwest

OTHER

collaborator

Stanford University

OTHER

collaborator

University of California, Davis

OTHER

collaborator

University of Florida

OTHER

collaborator

University of Iowa

OTHER

collaborator

University of Miami

OTHER

collaborator

University of Michigan

OTHER

collaborator

University of Minnesota

OTHER

collaborator

University of Oklahoma

OTHER

collaborator

University of Southern California

OTHER

collaborator

University of Utah

OTHER

collaborator

University of Washington

OTHER

collaborator

University of Wisconsin, Madison

OTHER

collaborator

Vanderbilt University

OTHER

collaborator

Vitreo Retinal Associates, PA

UNKNOWN

collaborator

University of Houston

OTHER

collaborator

Medical University of Graz

OTHER

collaborator

McGill University

OTHER

collaborator

Universität Tübingen

OTHER

collaborator

Radboud University Medical Center

OTHER

collaborator

University of Amsterdam

OTHER

collaborator

University Hospital, Basel, Switzerland

OTHER

collaborator

University College London Hospitals

OTHER

collaborator

Northwestern University

OTHER

collaborator

University of Pennsylvania

OTHER

lead

Johns Hopkins University

OTHER

NCT05537220 - Oral N-acetylcysteine for Retinitis Pigmentosa | Biotech Hunter | Biotech Hunter