Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-251 in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51 Skipping

UZ Leuven, Leuven

Murdoch Children's Research Institute, Parkville

CHR Citadelle, Liège

Samsung Medical Center, Seoul

Hospital Universitario Vall d'Hebron - PPDS, Barcelona

Hospital Sant Joan de Déu Universidad de Barcelona, Barcelona

UZ Gent, Ghent

Children's Hospital of Philadelphia, Philadelphia

Fondazione Serena Onlus - Centro Clinico NeMO, Milan

Ospedale San Raffaele S.r.l. - PPDS, Milan

Virginia Commonwealth University, Richmond

Rare Disease Research, LLC, Atlanta

Nationwide Children's Hospital, Columbus

Children's Hospital Colorado, Aurora

UCLA University California of Los Angeles, Los Angeles

University of California San Diego, La Jolla

Shriners Hospitals for Children Portland, Portland

UMass Memorial Medical Center, Worcester

UPMC Children's Hospital of Pittsburgh, Pittsburgh

University of Utah - PPDS, Salt Lake City

Children's Hospital at Westmead, Westmead

London Health Sciences Centre, London

Children's Hospital of Eastern Ontario, Ottawa

CHI [Children's Health Ireland] at Temple Street Children's University Hospital, Dublin

Fondazione Policlinico Universitario A Gemelli, Rome

Alder Hey Children's Hospital, Liverpool

Royal Victoria Infirmary, Newcastle upon Tyne

Leeds Teaching Hospitals NHS Trust, Leeds

Bristol Childrens Hospital, Bristol

Great Ormond Street Hospital, London