Caplacizumab and Immunosuppressive Therapy Without Firstline Therapeutic Plasma Exchange in Adults With Immune-mediated Thrombotic Thrombocytopenic Purpura

PHASE3CompletedINTERVENTIONAL
Enrollment

56

Participants

Timeline

Start Date

November 21, 2022

Primary Completion Date

December 26, 2024

Study Completion Date

December 26, 2024

Conditions
Thrombotic Thrombocytopenic Purpura
Interventions
DRUG

Caplacizumab

Lyophilized powder for solution for injection.

DRUG

Corticosteroids

Solution for injection or Tablet

BIOLOGICAL

anti-CD20 antibody

Solution for injection

Trial Locations (32)

1090

Investigational Site Number : 0400001, Vienna

5530

Investigational Site Number : 0560003, Yvoir

10117

Investigational Site Number : 2760006, Berlin

16132

Investigational Site Number : 3800006, Genova

20122

Investigational Site Number : 3800001, Milan

21287

Johns Hopkins University- Site Number : 8400007, Baltimore

28007

Investigational Site Number : 7240001, Madrid / Madrid

30625

Investigational Site Number : 2760004, Hanover

35233

University of Alabama- Site Number : 8400011, Birmingham

36100

Investigational Site Number : 3800004, Vicenza

37134

Investigational Site Number : 3800005, Verona

43210

The Ohio State University Comprehensive Cancer Center - Site Number : 8400001, Columbus

45122

Investigational Site Number : 2760003, Essen

50005

Investigational Site Number : 2030002, Hradec Králové

50937

Investigational Site Number : 2760002, Cologne

59037

Investigational Site Number : 2500005, Lille

60590

Investigational Site Number : 2760001, Frankfurt am Main

62500

Investigational Site Number : 2030001, Brno

75010

Investigational Site Number : 2500003, Paris

75012

Investigational Site Number : 2500001, Paris

76230

Investigational Site Number : 2500002, Bois-Guillaume

83100

Investigational Site Number : 3800003, Avellino

84106

University of Utah- Site Number : 8400009, Salt Lake City

27710-4000

Duke University Medical Center Site Number : 8400022, Durham

M5B 1W8

Investigational Site Number : 1240001, Toronto

128 00

Investigational Site Number : 2030003, Prague

04103

Investigational Site Number : 2760007, Leipzig

710-8602

Investigational Site Number : 3920003, Kurashiki-shi

350-0495

Investigational Site Number : 3920001, Iruma-gun

3818 TZ

Investigational Site Number : 5280002, Amersfoort

NW1 2PG

Investigational Site Number : 8260001, London

L7 8XP

Investigational Site Number : 8260002, Liverpool

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Sanofi

INDUSTRY

NCT05468320 - Caplacizumab and Immunosuppressive Therapy Without Firstline Therapeutic Plasma Exchange in Adults With Immune-mediated Thrombotic Thrombocytopenic Purpura | Biotech Hunter | Biotech Hunter