Data Analysis of Adult and Pediatric Participants With Acid Sphingomyelinase Deficiency (ASMD) on Early Access to Olipudase Alfa in France

CompletedOBSERVATIONAL
Enrollment

40

Participants

Timeline

Start Date

June 10, 2022

Primary Completion Date

December 31, 2024

Study Completion Date

December 31, 2024

Conditions
Acid Sphingomyelinase Deficiency (ASMD)
Interventions
DRUG

Olipudase alfa

GZ402665

Trial Locations (1)

Unknown

Investigational site in France, France

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Sanofi

INDUSTRY

NCT05359276 - Data Analysis of Adult and Pediatric Participants With Acid Sphingomyelinase Deficiency (ASMD) on Early Access to Olipudase Alfa in France | Biotech Hunter | Biotech Hunter