336
Participants
Start Date
May 15, 2022
Primary Completion Date
September 26, 2024
Study Completion Date
January 30, 2025
PTC857
PTC8657 will be administered as an oral solution twice a day.
Placebo
Matching placebo will be administered as an oral solution twice a day.
UZ Leuven, Leuven
Austin Health, Heidelberg
Calvary Health Care Bethlehem, Caulfield South
Royal Brisbane and Women's Hospital, Brisbane
Gold Coast Hospital, Southport
University Hospital Jena, Jena
AZ Sint-Lucas Gent, Ghent
AOU Citta Della Salute e Scienza, Torino
Charite - Universitatsmedizin - Berlin, Berlin
Lewis Katz School of Medicine at Temple Universtiy, Philadelphia
Istituti Clinici Scientifici Maugeri IRCCS, Milan
Istituto Auxolgoico Italiano, Milan
Universitaetsklinikum Schleswig-Holstein (UKSH) Campus Luebeck, Klinik fuer Neurologie, Praezisionsneurologie, Lübeck
Centro Clinico Nemo Brescia, Brescia
IRCCS Fondazione Mondino - Reparto Neuroncologia/Neuroinfiammazione, Pavia
Maggiore della Carita University Hospital, Neurology department, ALS center, Novara
Hannover Medical School, Hanover
Augusta University, Augusta
CHU de Bordeaux, Bordeaux
Holy Cross Hospital, Phil Smith Neuroscience Institute, Fort Lauderdale
University of South Florida - Carol and Frank Morsani Center for Advanced Healthcare, Tampa
CHU Gui de Chauliac (Pharmacie Saint-Eloi & Gui de Chauliac, Hopital Saint-Eloi), Montpellier
Azienda Ospedaliero Universitaria di Modena, Modena
Hospital Universitario y Politecnico La Fe, Valencia
Henry Ford Health System Department of Neurology, Detroit
Medical College of Wisconsin, Milwaukee
CHRU Lille - Hôpital Roger Salengro, Lille
University hospital Brno, Department of Neurology, Brno
CHU Gabriel Montpied, Clermont-Ferrand
University of Kansas Medical Center (KUMC) - Landon Center on Aging, Kansas City
Neurology Associates, P.C. / Somnos Clinical Research, Lincoln
Hôpital Neurologique Pierre Wertheimer, Bron
Nerve and Muscle Center of Texas, Houston
National Neuromuscular Research Institute, Austin
CHU Dupuytren 1 Limoges, Limoges
University of Ulm, Dept. of Neurology, Ulm
"ALS Clinical Research Center, University Hospital Policlinico P Giaccone", Palermo
Norrlands universitetssjukhus Neurologens Forskningsavdelning, Umeå
UC Irvine Health ALS and Neuromuscular Center, Orange
Forbes Norris MDA/ALS Research Center at California Pacific Medical Center, San Francisco
Providence Brain and Spine Institute, Portland
University of Nebraska Medical Center, Omaha
STAT Research S.A., Ciudad Autónoma de Buenos Aires
Iadin Srl., Buenos Aires
Hospital Ramos Mejía, Buenos Aires
FORBELI s.r.o., Prague
CRMR SLA - MNM du CHU de Nice, Nice
Policlinico Umberto I, Roma
PTC Clinical Site, Japanese City
UMC Utrecht, Utrecht
Centrum Medyczne Neuro Protect, Warsaw
City Clinic Research Sp. Z o.o, Warsaw
Unidad Neuromuscular. Servicio de Neurologia Hospital Universitari Vall d'Hebron, Barcelona
H. St Pau, Barcelona
Skanes universitetssjukhus, VE Neurologi, Malmo
Lead Sponsor
PTC Therapeutics
INDUSTRY