175
Participants
Start Date
July 6, 2022
Primary Completion Date
August 31, 2026
Study Completion Date
August 31, 2026
Sevasemten 10 mg
Sevasemten is administered orally once per day
Sevasemten 5 mg
Sevasemten is administered orally once per day
Sevasemten 12.5 mg
Sevasemten is administered orally once per day
Placebo
Placebo is administered orally once per day
Optimal Clinical Trials, Auckland
Centre Hospitalier Régional de la Citadelle, Liège
University Hospital Gent, Ghent
Centre de Reference des Maladies Neuromusculaires et de la SLA - AP-HM Hopital de La Timone, Marseille
University of Rochester Medical Center, Rochester
University of Pittsburgh, Pittsburgh
University of Pennsylvania, Philadelphia
Hospital Universitario Donostia, Donostia / San Sebastian
Fondazione IRCCS Ca'Granda Ospedale Maggiore Policlinico di Milano, Milan
Kennedy Krieger Institute, Baltimore
Virginia Commonwealth University Health, Richmond
Rare Disease Research, LLC NC, Hillsborough
Rare Disease Research, Atlanta
University of Florida, Gainesville
Azienda Ospedale - Università Padova, Padua
Nationwide Children's Hospital, Columbus
CHU de Nantes, Nantes
University of Cincinnati Gardner Neuroscience Institute, Cincinnati
Hospital Universitari i Politecnic La Fe, Valencia
Indiana University School of Medicine, Indianapolis
Schneider Children's Hospital of Israel, Petah Tikva
University of Iowa, Iowa City
University of Minnesota, Minneapolis
Northwestern University, Chicago
Washington University School of Medicine, St Louis
University of Kansas Medical Center, Kansas City
Arkansas Children's Hospital, Little Rock
AP-HP Hopital Pitie-Salpetriere, Paris
Neurology Rare Disease Center, Denton
National Neuromuscular Research Institute, Austin
UC Denver, Aurora
Klinikum der Ludwig-Maximilians-Universitaet Muenchen, Munich
UCLA Medical Center, Los Angeles
Hadassah University Hospital, Jerusalem
UC San Diego, La Jolla
UC Irvine Medical Center, Orange
Stanford Neuroscience Health Center, Palo Alto
UC Davis Medical Center, Sacramento
University of Massachusetts Memorial Medical Center, Worcester
St Vincent's Hospital Melbourne, Fitzroy
Universitaire Ziekenhuizen Leuven, Leuven
Rigshospitalet, Copenhagen
CHU de Nice - Hopital Pasteur 2 - Centre de reference des Maladies Neuromusculaires, Nice
Fondazione Policlinico Universitario A. Gemelli IRCCS - Universita Cattolica del Sacro Cuore, Rome
Leids Universitair Medisch Centrum, Leiden
Hospital Universitario Vall d'Hebron, Barcelona
Hospital Universitari de Bellvitge, Barcelona
University College London Hospital, London
St. George's University Hospitals NHS Foundation Trust, London
Newcastle Freeman Hospital, Newcastle
Salford Royal Hospital, Salford
Lead Sponsor
Collaborators (2)
Medpace, Inc.
INDUSTRY
ImagingNMD
UNKNOWN
SYSNAV
INDUSTRY
Edgewise Therapeutics, Inc.
INDUSTRY