104
Participants
Start Date
May 3, 2022
Primary Completion Date
May 15, 2026
Study Completion Date
December 6, 2027
Venglustat (GZ402671)
Tablet; Oral
Agalsidase alfa
Concentrate for solution for infusion; IV infusion
Agalsidase beta (GZ419828)
Powder for concentrate for solution for infusion; IV infusion
Migalastat
Hard capsules; Oral
Investigational Site Number : 1580001, Taipei
Investigational Site Number : 1580003, Taichung
Investigational Site Number : 2080001, Copenhagen
Investigational Site Number : 5780001, Bergen
Investigational Site Number : 0400001, Graz
Investigational Site Number : 2760003, Berlin
Maryam Banikazemi, MD- Site Number : 8400001, Hawthorne
Investigational Site Number : 3800001, Milan
Lysosomal and Rare Disorders Research and Treatment Center (LDRTC)- Site Number : 8400004, Fairfax
Investigational Site Number : 7240002, Madrid
Emory University School of Medicine - Atlanta- Site Number : 8400009, Atlanta
Investigational Site Number : 7920002, Istanbul
University of Alabama -The Kirklin Clinic- Site Number : 8400010, Birmingham
Investigational Site Number : 7240001, Pontevedra
Investigational Site Number : 3800004, Bologna
Investigational Site Number : 7920003, İzmit
Investigational Site Number : 4100002, Yangsan
Investigational Site Number : 2760005, Mainz
Ann & Robert H. Lurie Children's Hospital of Chicago- Site Number : 8400005, Chicago
Investigational Site Number : 2760004, Hochheim am Main
Renal Disease Research Institute- Site Number : 8400012, Dallas
Investigational Site Number : 3800002, Naples
Investigational Site Number : 3800003, Naples
University of Utah Health Hospital- Site Number : 8400006, Salt Lake City
University of California Los Angeles Medical Center- Site Number : 8400008, Los Angeles
Investigational Site Number : 2500001, Garches
Investigational Site Number : 2760001, Würzburg
Investigational Site Number : 1560002, Beijing
Investigational Site Number : 1560005, Beijing
Investigational Site Number : 1560003, Shanghai
Investigational Site Number : 1560007, Guangzhou
Investigational Site Number : 1560001, Chengdu
Investigational Site Number : 1240003, Calgary
Investigational Site Number : 1240006, Edmonton
Investigational Site Number : 1240002, Vancouver
Investigational Site Number : 1240005, Toronto
Investigational Site Number : 2030001, Prague
Investigational Site Number : 3000002, Athens
Investigational Site Number : 3000003, Athens
Investigational Site Number : 3000001, Heraklion
Investigational Site Number : 3920006, Sapporo
Investigational Site Number : 3920007, Kagoshima
Investigational Site Number : 3920003, Kagoshima
Investigational Site Number : 3920005, Kawasaki
Investigational Site Number : 3920002, Sendai
Investigational Site Number : 3920004, Fukuoka
Investigational Site Number : 3920001, Tokyo
Investigational Site Number : 5280001, Amsterdam
Investigational Site Number : 6160003, Lodz
Investigational Site Number : 6160001, Krakow
Investigational Site Number : 4100001, Seoul
Investigational Site Number : 7240003, Alicante
Investigational Site Number : 7920001, Ankara
Investigational Site Number : 8260001, London
Lead Sponsor
Sanofi
INDUSTRY