55
Participants
Start Date
June 17, 2022
Primary Completion Date
January 14, 2025
Study Completion Date
October 31, 2027
Pegvaliase
Pegvaliase 2.5mg/10mg/20mg/40mg/60mg self-administered from 1 time up to 7 times a week
Diet Only
Diet Control
University of Pittsburgh Medical Center, Pittsburgh
University of Virginia School of Medicine, Charlottesville
University of South Florida, Tampa
University of Kentucky College of Medicine, Lexington
IU Health University Hospital, Indianapolis
Children's Hospital of Wisconsin, Milwaukee
Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago
Arkansas Children's Hospital, Little Rock
McGovern Medical School, University of Texas Health Science Center at Houston (UTHealth), Houston
Children's Hospital of Colorado, Aurora
University of Utah Medical Center, Salt Lake City
Phoenix Children's Hospital, Phoenix
Boston Children's Hospital, Boston
Charité - Universitätsmedizin Berlin, Berlin
Universitätsklinikum Hamburg-Eppendorf, Hamburg
Universitat Mainz, Mainz
Lead Sponsor
BioMarin Pharmaceutical
INDUSTRY