402
Participants
Start Date
March 29, 2022
Primary Completion Date
December 31, 2026
Study Completion Date
December 31, 2026
Risdiplam
Risdiplam taken by participants as prescribed by their physician.
SMA-DAT Application and ADAM Sensor
Participants will perform a programmed selection of SMA-DAT tasks while wearing the ADAM Sensor.
NYU Hospital for Joint Diseases, New York
Columbia University Med Center, New York
Penn State Milton S. Hershey Medical Center, Hershey
Childrens Hospital of Philadelphia, Philadelphia
Medstar Georgetown University Hospital, Washington D.C.
Children's National Hospital, Washington D.C.
University of Virginia Children?s Hospital, Charlottesville
UBC (Remote Coordinating Center, no physical facility), Morgantown
Rare Disease Research, LLC, Atlanta
Advent Health Orlando, Winter Park
Nemour's Children's Hospital, Florida, Orlando
All Children's Research Institute, Inc., St. Petersburg
Norton Children's Hospital, Louisville
University of Kentucky Medical Center, Lexington
Cincinnati Childrens Hospital, Cincinnati
University of Michigan Pediatric Rehabilitation Center, Ann Arbor
Helen DeVos Children's Hospital at Spectrum Health, Grand Rapids
Childrens Hospital of Wisconsin, Milwaukee
Gillette Children's Specialty Healthcare, Minnetonka
Mayo Clinic, Rochester
Washington University;Wash Uni. Sch. Of Med, St Louis
University of Kansas Medical Center, Kansas City
University of Arkansas for Medical Sciences, Little Rock
Neurology & Neuromuscular Care Center, Denton
Methodist Children's Hospital of South Texas, San Antonio
Central Texas Neurology Consultants, Round Rock
University of Texas at Austin Health sciences, Dell Medical School, Austin
University of Colorado, Aurora
University Of Utah, Salt Lake City
Barrow Neurological Institute, Phoenix
Phoenix Children's Hospital, Phoenix
Children's Hospital Los Angeles, Los Angeles
Loma Linda University Health Care, Loma Linda
University California - Irvine, Orange
Valley Children's Hospital, Madera
University of California Davis Medical Center, Sacramento
MultiCare Health System Institute for Research and Innovation, Tacoma
Massachusetts General Hospital, Boston
Instituto de Rehabilitación del Caribe, Santurce
Lead Sponsor
Genentech, Inc.
INDUSTRY