A Study to Evaluate the Safety and Tolerability of ALN-APP in Patients With EOAD

PHASE1RecruitingINTERVENTIONAL
Enrollment

60

Participants

Timeline

Start Date

February 4, 2022

Primary Completion Date

March 28, 2029

Study Completion Date

March 28, 2029

Conditions
Early-Onset Alzheimer Disease
Interventions
DRUG

ALN-APP

ALN-APP will be administered intrathecally (IT)

DRUG

Placebo

Placebo will be administered IT

Trial Locations (8)

46202

RECRUITING

Clinical Trial Site, Indianapolis

92037

WITHDRAWN

Clinical Trial Site, San Diego

92103

RECRUITING

Clinical Trial Site, San Diego

Unknown

RECRUITING

Clinical Trial Site, Toronto

RECRUITING

Clinical Trial Site, Montreal

RECRUITING

Clinical Trial Site, Amsterdam

RECRUITING

Clinical Trial Site, London

RECRUITING

Clinical Trial Site, Sheffield

Sponsors
All Listed Sponsors
lead

Alnylam Pharmaceuticals

INDUSTRY