43
Participants
Start Date
April 18, 2022
Primary Completion Date
October 2, 2025
Study Completion Date
October 30, 2026
Venglustat
tablet; oral
imiglucerase
sterile lyophilized product; intravenous
Hospital de Ninos - Investigational Site Number: 320001, Buenos Aires
National Taiwan University Hospital-Investigational Site Number: 1580001, Taipei
Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico - Investigational Site Number : 3800003, Milan
Lysosomal & Rare Disorders Research & Treatment Center, Inc - Investigational Site Number: 8400001, Fairfax
Istanbul University Medical Faculty Hospital-Investigational Site Number : 7920004, Istanbul
University of Iowa - Investigational Site Number: 8400002, Iowa City
SphinCS GmbH - Investigational Site Number: 2760001, Hochheim am Main
47-87, boulevard de l'hôpital - Investigational Site Number: 2500003, Paris
Hopital Necker - Investigational Site Number: 2500001, Paris
Texas Oncology - Medical City Dallas Site Number : 8400008, Dallas
"Azienda Ospedaliera Universitaria (AOU) Federico II - Investigational Site Number: 3800002", Napoli
Peking Union Medical College Hospital - Investigational Site Number: 1560001, Beijing
Xinhua Hospital - Investigational Site Number: 1560004, Shanghai
The First Affiliated Hospital - Investigational Site Number: 1560002, Guangzhou
Yale University School of Medicine - Investigational Site Number: 8400003, New Haven
Children's Hospital Research Institute of Manitoba - Investigational Site Number: 1240001, Winnipeg
Debreceni Egyetem, Klinikai Központ, Reumatológiai Klinika - Investigational Site Number: 3480001, Debrecen
Odawara Municipal Hospital-Investigational Site Number : 3920002, Odawara
Tohoku University School of Medicine - Investigational Site Number: 3920001, Sendai
Cukurova University Medical School Hospital-Investigational Site Number : 7920001, Adana
Gazi University Medical Hospital-Investigational Site Number : 7920002, Ankara
Investigational Site Number : 8260001, London
Lead Sponsor
Sanofi
INDUSTRY