102
Participants
Start Date
June 21, 2022
Primary Completion Date
April 15, 2025
Study Completion Date
April 15, 2025
Vatiquinone
Vatiquinone will be administered per dose and schedule specified in the arm description.
Columbia University Medical Center - CUMC, New York
Children's Hospital of Philadelphia - CHOP, Philadelphia
Children's National, Washington D.C.
The Johns Hopkins University, Baltimore
Hospital Universitario 12 de Octubre, Madrid
Hospital Ruber Internacional, Madrid
Medical University of South Carolina - MUSC, Charleston
Child Neurology Center of Northwest Florida, Gulf Breeze
CHU Montpellier - Hopital Saint-Eloi, Montpellier
Cleveland Clinic, Cleveland
Akron Children's Hospital, Akron
Chu Angers, Angers
Hôpital de Hautepierre - Hôpitaux Universitaires de Strasbourg, Strasbourg
Hopital Necker-Enfants Malades, Paris
Baylor College of Medicine, Houston
UT Health The University of Texas, Houston
University of California, San Diego Altman Clinical and Translational Research Institute, La Jolla
Stanford University, Stanford
Seattle Children Hospital, Seattle
Yale Medicine, New Haven
Ospedale Pediatrico Bambino Gesù, Roma
PTC Clinical Site, Japanese City
Instytut Pomnik - Centrum Zdrowia Dziecka, Warsaw
Hospital Sant Joan de Déu, Barcelona
Great Ormond Street Hospital for Children NHS Foundation Trust, London
The Newcastle Upon Tyne Hospitals NHS Foundation Trust, Newcastle upon Tyne
Lead Sponsor
PTC Therapeutics
INDUSTRY