122
Participants
Start Date
March 11, 2022
Primary Completion Date
December 7, 2025
Study Completion Date
January 4, 2027
Venglustat (GZ402671)
Pharmaceutical form: Tablet Route of administration: Oral
Placebo
Pharmaceutical form: Tablet Route of administration: Oral
Investigational Site Number: 0400001, Vienna
Investigational Site Number: 2080001, Copenhagen
Investigational Site Number : 0360001, Parkville
Investigational Site Number: 5780001, Bergen
Investigational Site Number : 7560001, Zurich
Westchester Medical Center Healthcare Corporation- Site Number : 8400001, Hawthorne
Children's Hospital Of Pittsburgh- Site Number : 8400009, Pittsburgh
Fondazione IRCCS San Gerardo dei Tintori, S.C. Nefrologia - Clinica Nefrologica_Investigational Site Number: 3800002, Monza
Lysosomal and Rare Disorders Research and Treatment Center_Investigational Site Number: 8400004, Fairfax
Institutul Clinic Fundeni_Investigational Site Number: 6420001, Bucharest
Emory Genetics- Site Number : 8400010, Atlanta
Advent Health Orlando_Investigational Site Number: 8400008, Orlando
Nephrology Clinic at Kirklin Clinic of UAB Hospital_Investigational Site Number: 8400011, Birmingham
IRCCS Policlinico di Sant'Orsola_Investigational Site Number : 3800005, Bologna
Investigational Site Number : 7920002, İzmit
Cleveland Clinic Site Number : 8400016, Cleveland
Investigational Site Number : 7920004, Malatya
Investigational Site Number : 2760005, Mainz
"Hospital Universitario Dr. José Eleuterio González Departamento de Genética Centro Universitario contra el cáncer_Investigational Site Number: 4840001", Monterrey
ISphinCS GmbH_Investigational Site Number: 2760004, Hochheim am Main
Renal Disease Research Institute, An affiliate of: Dallas Nephrology Associates_Investigational Site Number: 8400012, Dallas
"Azienda Ospedaliera Universitaria Federico II, U.O. di Nefrologia- Diparimento di Sanità Pubblica_Investigational Site Number: 3800001", Napoli
Investigational Site Number: 2760003, München
University Of Utah Health Sciences Center- Site Number : 8400005, Salt Lake City
UCLA Medical Center_Investigational Site Number: 8400006, Los Angeles
Azienda Ospedaliera Universitaria_Investigational Site Number: 3800003, Palermo
Investigational Site Number : 2500001, Garches
University of California Irvine Medical Center- Site Number : 8400019, Orange
Investigational Site Number: 2760001, Würzburg
No.8, Xishiku Street, Xicheng District_Site Number: 1560001, Beijing
No.197,2nd Ruijin road, Huangpu district_Site Number: 1560003, Shanghai
Investigational Site Number : 1560006, Zhengzhou
Cincinnati Children's Hospital Medical Center - PIN- Site Number : 8400013, Cincinnati
Fundacion Cori para la Investigación y Prevención del Cancer_Investigational Site Number: 0320002, La Rioja
Instituto de Investigaciones Clínicas Quilmes (IICQ) SRL_Investigational Site Number: 0320003, Quilmes
Hospital de Clínicas de Porto Alegre_Investigational Site Number: 0760001, Porto Alegre
Instituto de Genética e Erros Inatos do Metabolismo - IGEIM- Site Number : 0760002, São Paulo
M.A.G.I.C Calgary LTD_Investigational Site Number: 1240003, Calgary
Medicine Dalhousie University_Investigational Site Number : 1240001, Halifax
University Health Network_Investigational Site Number : 1240005, Toronto
No.85 South Jiefang road, Yingze District_Site Number: 1560004, Taiyuan
Investigational Site Number: 2460001, Turku
Investigational Site Number : 3000003, Athens
University Hospital of Heraklion_Investigational Site Number: 3000001, Heraklion
University Hospital of Ioannina_Investigational Site Number: 3000002, Ioannina
Fondazione Policlinico Universitario_Investigational Site Number: 3800004, Roma
Investigational Site Number : 3920005, Kawasaki
Fukuoka University Hospital_Investigational Site Number: 3920004, Fukuoka-shi, Fukuoka
The Jikei University Hospital_Investigational Site Number: 3920003, Minato-ku, Tokyo
Tohoku University Hospital_Investigational Site Number: 3920001, Sendai-shi, Miyagi
Odette del Carmen DIAZ-AVENDAÑO Clinstile, S.A. de C.V. Durango_Investigational Site Number: 4840002, Mexico City
Investigational Site Number : 6160002, Poznan
Investigational Site Number : 6160004, Rzeszów
Investigational Site Number: 6160003, Wroclaw
Investigational Site Number : 7920001, Ankara
Investigational Site Number: 8260001, Cambridge
Investigational Site Number: 8260002, London
Investigational Site Number : 8260003, Salford
Lead Sponsor
Sanofi
INDUSTRY