Fabry Patient's Experience Of PegunigaLsidasE Alfa Monthly Infusion

CompletedOBSERVATIONAL
Enrollment

23

Participants

Timeline

Start Date

January 26, 2022

Primary Completion Date

August 31, 2022

Study Completion Date

August 31, 2022

Conditions
Fabry Disease
Interventions
OTHER

Interview

"During each interview, patients will be asked questions to collect demographic and clinical information, and asked a set of open-ended questions with probes to describe their experiences with Fabry disease (symptomology and impacts on patient's lives \[i.e., activities of daily living, school/work, ability to take holidays/vacation\]), and pegunigalsidase alfa treatment (experience of infusions and schedule) and their experience of change in symptoms and impacts over the BRIGHT-F51 clinical study.~A semi-structured discussion guide will be used to conduct the approximately 60-minute interviews. The use of open-ended questions avoids bias and questions will not be read verbatim to allow for a free-flowing discussion."

Trial Locations (12)

2100

#50, Copenhagen

2650

#22, Antwerp

22030

#01, Fairfax

30322

#03, Atlanta

35233

#02, Birmingham

49525

#11, Grand Rapids

52242

#04, Iowa City

75246

#06, Dallas

80131

#56, Napoli

84132

#05, Salt Lake City

CB2 2QQ

#28, Cambridge

NW3 2QG

#07, London

All Listed Sponsors
collaborator

Protalix

INDUSTRY

collaborator

Iqvia Pty Ltd

INDUSTRY

lead

Chiesi Farmaceutici S.p.A.

INDUSTRY