102
Participants
Start Date
April 29, 2022
Primary Completion Date
September 30, 2024
Study Completion Date
October 31, 2024
Elamipretide
60 mg of elamipretide administered as once daily 0.75 mL subcutaneous injections for 48 weeks
Placebo
Placebo administered as once daily 0.75 mL subcutaneous injections for 48 weeks
University of Auckland - Auckland City Hospital, Neurology Department, Auckland
Semmelweis Egyetem Genomikai Medicina es Ritka Betegsegek, Budapest
Royal North Shore Hospital Neurology, Sydney
Calvary Health Care Bethlehem, Parkdale
Helse Bergen HF, Bergen
Radboud University Medical Center, Nijmegen
University of Pécs, Department of Neurology Klinikai Kozpont - neurologiai Klinika, Pécs
Hospital de la Sta Creu i Sant Pau, Barcelona
Hospital Clinic de Barcelona, Barcelona
Columbia University Medical Center College of Physician and Surgeon, New York
University of Pittsburgh School of Medicine Children's Hospital of Pittsburgh of UPMC Department of Genetics, Pittsburgh
The Children's Hospital of Philadelphia, Philadelphia
Istituto Nazionale Neurologico Carlo Besta, Milan
University of Brescia, NeMO Clinical Center for Neuromuscular Diseases, Gussago
Hospital Universitario 12 de Octubre, Madrid
Rare Disease Research, LLC, Atlanta
Akron Children's Hospital, Akron
Hospital la Fe de Valencia, Valencia
Azienda Ospedaliero Universitario Pisana, Dipartimento Ambientale di Neuroscienze, Pisa
Washington University School of Medicine, St Louis
UT Health,Center for the Treatment of Pediatric Neurodegenerative Disease, Houston
Department of Neurology, University Clinics Munich, Munich
University of California, San Diego, San Diego
Azienda Ospedaliero Universitaria Policlinico G. Martino, Messina
Massachusetts General Hospital, Boston
Universitaetsklinikum Carl Gustav Carus Dresden Neurologie, Dresden
Univ of Tubingen, Hertie Institute for Clinical Brain Research, Tübingen
IRCCS Institute of Neorological Sciences of Bologna Bellaria Hospital, Bologna
Istituto di Neurologia, Fondazione Policlinico Universitario A. Gemelli, Università Cattolica del Sacro Cuore, Rome
University of Cambridge, Department of Clinical Neurosciences, Cambridge
Queen Square Centre for Neuromuscular Diseases The National Hospital for Neurology and Neurosurgery, London
Newcastle upon Tyne Hospitals Freeman Hospital, Newcastle
Stealth BioTherapeutics Inc.
INDUSTRY