188
Participants
Start Date
April 14, 2022
Primary Completion Date
December 18, 2024
Study Completion Date
December 18, 2024
Apitegromab
Apitegromab is a fully human anti-proMyostatin monoclonal antibody (mAb) of the immunoglobulin G4 (IgG4)/lambda isotype that specifically binds to human pro/latent myostatin with high affinity inhibiting myostatin activation. SRK-015 was administered every 4 weeks by intravenous (IV) infusion.
Placebo
Placebo was administered every 4 weeks by intravenous (IV) infusion.
UZ Leuven, Leuven
Universitair Medisch Centrum Utrecht, Utrecht
Chr de La Citadelle, Liège
UZ Gent, Ghent
Columbia University, SMA Clinical Research Center, New York
Childrens Hospital of Philadelphia, Philadelphia
Foundation I.R.C.C.S. Carlo Besta Neurological Institute, Milan
ASST Grande Ospedale Metropolitano Niguarda, Milan
The Johns Hopkins University, Baltimore
Children's Hospital of The King's Daughters, Norfolk
Wake Forest Baptist Medical Center, Winston-Salem
CHU Toulouse - Hopital des Enfants, Toulouse
Nemours Children's Hospital, Orlando
Children's of Alabama, Birmingham
St. Jude Children's Research Hospital, Memphis
Nationwide Children's Hospital, Columbus
Universitätsklinikum Essen, Essen
Helen DeVos Children's Hospital, Grand Rapids
University of Iowa, Iowa City
Universitätsklinikum Bonn, Bonn
University of Wisconsin School of Medicine and Public Health, Madison
Gillette Children's Specialty Healthcare, Saint Paul
CHU Lille - Hôpital Jeanne de Flandre, Lille
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
Washington University School of Medicine in St. Louis, St Louis
University of Kansas Medical Center, Kansas City
Hôpital Armand Trousseau, I-Motion, Paris
Children's Medical Center Dallas, Dallas
Universitaetsklinikum Freiburg, Freiburg im Breisgau
Children's Hospital Colorado, Aurora
Dr. von Haunersches Kinderspital, Munich
University of Utah, Salt Lake City
Phoenix Children's Hospital, Phoenix
Children's Hospital of Los Angeles, Los Angeles
Rady's Children's Hospital/UCSD, San Diego
Stanford University Medical Center, Palo Alto
Oregon Health & Sciences University, Portland
Seattle Children's Hospital, Seattle
A.O.U Policlinico G. Martino, Messina
Boston Children's Hospital, Boston
IRCCS Istituto Giannina Gaslini, Genoa
Hospital Sant Joan de Déu, Barcelona
Hospital Universitario y Politécnico La Fe, Valencia
Great Ormond Street Hospital for Children NHS Foundation Trust, London
Centro Clinico Nemo Pediatrico Policlinico A. Gemelli-Università Cattolica Sacro Cuore, Roma
Uniwersyteckie Centrum Kliniczne w Gdańsku, Gdansk
Uniwersytet Medyczny im. Karola Marcinkowskiego w Poznaniu, Poznan
Instytut Pomnik - Centrum Zdrowia Dziecka: CZD Warszawa, Warsaw
Leeds Teaching Hospitals NHS Trust, Leeds
University of Oxford, Oxford
Scholar Rock, Inc.
INDUSTRY