NCT05154890 - A Multiple Ascending Dose Study of ACN00177 (Pegtarviliase) in Subjects With CBS Deficiency | Biotech Hunter

Enrollment

Participants

Timeline

Start Date

May 13, 2021

Primary Completion Date

April 21, 2023

Study Completion Date

April 21, 2023

Conditions

Homocystinuria Due to Cystathionine Beta-Synthase Deficiency

Interventions

DRUG

Pegtarviliase IV

Administered IV

DRUG

Pegtarviliase SC

Administered SC

Trial Locations (9)

UT Southwestern Medical Center, Dallas

Westmead Hospital, Westmead

Royal Children's Hospital, Parkville

Royal Melbourne Hospital, Parkville

University Hospitals Birmingham NHS, Birmingham

Great Ormond Street Hospital, London

Guy's and St Thomas' Hospital NHS Foundation Trust, London

University College London, London

Salford Royal NHS Foundation Trust, Salford