153
Participants
Start Date
March 24, 2022
Primary Completion Date
April 21, 2026
Study Completion Date
November 2, 2029
Concizumab
"Participants in Arm 1 will be assigned to concizumab prophylaxis starting with a loading dose on treatment day 0 followed by daily injections of an individual maintenance dose.~Participants in Arm 2 will be assigned to concizumab prophylaxis with daily injections of an individual maintenance dose."
Saint George Hospital University Medical Center, Beirut
PHI University Clinic for Children's Diseases Skopje, Skopje
Hospital Nini, Tripoli
UMHAT Tsaritsa Yoanna-ISUL EAD, Sofia
Charlotte Maxeke Johannesburg Academic Hospital, Parktown, Johannesburg
UMHAT Sveti Georgi EAD, Plovdiv, Clinic of Pediatrics, Plovdiv
"UMHAT Sveta Marina EAD", Varna
King Chulalongkorn Memorial Hospital - Pediatric Hematology-Oncology, Bangkok
King Chulalongkorn Memorial Hospital_Bangkok_0, Bangkok
Ramathibodi Hospital, Bangkok
Hospital Pulau Pinang, George Town
Siriraj Hospital - Hematology and Oncology, Bangkok
Tallinn Children's Hospital, Tallinn
Haematology and Blood Bank Department, Algiers
St Christopher Hosp for Child, Philadelphia
Hospital Sultanah Nur Zahirah, Kuala Terengganu
CHU Constantine BEN BADIS/ Hematology department, Constantine
ECU Sickle Cell Comp Clinic, Greenville
Hospital Universitario La Paz, Madrid
Hospital Regional Universitario de Málaga, Málaga
Hospital Virgen de la Arrixaca - Hematología, El Palmar
Memorial Health University Medical Center, Savannah
Arnold Palmer Children's Hospital, Orlando
Sunpasitthiprasong Hospital, Ubon Ratchathani
Ege Universitesi Tip Fakultesi, Izmir
Azienda Ospedaliera di Padova, Padua
Vanderbilt Hemostasis Treatment Clinic, Nashville
Azienda Ospedaliera-Universitaria Parma, Parma
Nationwide Children's Hospital, Columbus
Indiana Hemophilia-Thromb Ctr, Indianapolis
Dipartimento di Ematologia Univ. Firenze, Florence
Hospital Tunku Azizah, Kampung Baru
'Ippokrateio' General Hospital of Thessaloniki, Thessaloniki
Ondokuz Mayis University Medical Faculty Ped. Haematology, Samsun
Childrens Hospital of Chicago, Chicago
The Children's Mercy Hospital, Kansas City
Children's Nebraska, Omaha
Children's Hosp-New Orleans, New Orleans
Centre Hospitalier Metropole Savoie, Chambéry
Ap-Hp-Hopital Necker-1, Paris
Cook Children's Hospital-Hematology-Oncology, Fort Worth
Texas Children's Hospital_Houston, Houston
Rady Childrens Hosp San Diego, San Diego
Sarawak General Hospital, Kuching
Ap-Hp-Hopital de Bicetre-1, Le Kremlin-Bicêtre
"A.O.U policlinico G. Rodolico-San Marco", Catania
Post Graduate Institute of Child Health, Noida
J K Lon Hospital, Jaipur
Nirmal Hospital Pvt. Ltd., Surat
Seth GS Medical College & KEM Hospital, Mumbai
K.J Somaiya Hospital and Research Centre, Mumbai
MCGM - Comprehensive Thalassemia Care, Mumbai
Spitalul Clinic Judetean De Urgenta Bihor, Oradea
Sahyadri Super Speciality Hospital, Pune
SSSH_Dept. of Clinical Haematology & Haemato Oncology, Kolhāpur
S.C.B. Medical College, Cuttack
Guwahati Medical College, Guwahati
BC Children's Hospital, Vancouver
McMaster Children's Hospital, Hamilton
Aghia Sophia Childrens' Hospital, Athens
'Ippokrateio' General Hospital of Thessaloniki, Thessaloniki
St. Marianna University School of Medicine Hospital_Pediatrics, Kanagawa
Saitama Children's Med Centre_Hematology-Oncology, Saitama
Centre of Oncology and Hematology, Vilnius University, Vilnius
Klinisk forskningspost, Oslo
Uniwersytecki Szpital Kliniczny im. J.Mikulicza-Radeckiego, Wroclaw
Uniwersyteckie Centrum Kliniczne, Gdansk
Uniwersytecki Szpital Dzieciecy, Dzial Krwiolecznictwa, Lublin
Uniwersyteckie Centrum Kliniczne WUM, Warsaw
Hospital Vall d'Hebron, Barcelona
Koagulationscentrum, Gothenburg
Gazi University, Ankara
Acibadem Adana Hastanesi, Adana
Birmingham Children's Hospital, Birmingham
University Hospitals Bristol & Weston NHS Foundation Trust, Bristol
Evelina London Children's Hospital, London
Great Ormond Street Hospital for Children, London
Lead Sponsor
Novo Nordisk A/S
INDUSTRY