64
Participants
Start Date
October 13, 2021
Primary Completion Date
December 31, 2025
Study Completion Date
June 30, 2027
Sirolimus
The investigational drug product to be used in this study is sirolimus, provided in oral suspension.
Placebo
Matching placebo
RECRUITING
University of North Carolina at Chapel Hill, Chapel Hill
RECRUITING
University of Alabama at Birmingham, Birmingham
RECRUITING
Cincinnati Children's Hospital Medical Center, Cincinnati
RECRUITING
Lurie Children's Hospital of Chicago, Chicago
RECRUITING
Washington University -- St. Louis, St Louis
RECRUITING
University of Texas HSC at Houston, Houston
RECRUITING
Children's Hospital Colorado, Aurora
RECRUITING
University of California at Los Angeles, Los Angeles
RECRUITING
Stanford University, Palo Alto
RECRUITING
Seattle Children's Hospital, Seattle
RECRUITING
Boston Children's Hospital, Boston
Darcy Krueger
OTHER