A Study of PTC923 in Participants With Phenylketonuria

PHASE3CompletedINTERVENTIONAL
Enrollment

157

Participants

Timeline

Start Date

September 30, 2021

Primary Completion Date

April 3, 2023

Study Completion Date

May 3, 2023

Conditions
Phenylketonuria
Interventions
DRUG

PTC923

PTC923 powder for oral use will be suspended in water or apple juice prior to administration.

DRUG

Placebo

Placebo matching to PTC923

Trial Locations (43)

159

Pediatric Surgery Center, Tbilisi

1130

Cukurova Üniversity Balcali Hospital Health Application and Research Center, Adana

2145

Westmead Hospital, Westmead

3050

Royal Melbourne Hospital, Melbourne

3310

Grupo Médico Camino SC, Benito Juárez

6230

Hacettepe University Medical Faculty, Altındağ

6560

Gazi Üniversitesi Tıp Fakültesi, Yenimahalle

8950

Hospital Sant Joan de Déu, Barcelona

15224

UPMC Children's Hospital of Pittsburgh, Pittsburgh

19104

The Children's Hospital of Philadelphia, Philadelphia

20246

University Children's Hospital Hamburg Eppendorf (Kinder-UKE) Klinik für Kinder- und Jugendmedizin (Kinder-UKE), Hamburg

28034

Hospital Universitario Ramón y Cajal, Madrid

32608

UF College of Medicine, Department of Pediatrics Division of Genetics and Metabolism, Gainesville

34098

İstanbul Üniversitesi Cerrahpaşa Tıp Fakültesi, Fatih

35100

Ege University Faculty of Medicine Children Hospital, Bornova

35128

Division of Inherited Metabolic Diseases, Azienda Ospedaliera-Università Padova, Padua

37000

Bretonneau Hospital - CHRU de Tours, Tours

37044

CHRU de Tours- Hôpital Pédiatrique de Clocheville, Tours

44670

PanAmerican Clinical Research, Guadalajara

46202

Indiana University School of Medicine, Indianapolis

48149

Universitätsklinikum Münster, Münster

53226

Medical College of Wisconsin, Milwaukee

69120

Universitätsklinikum Heidelberg / Zentrum für Kinder- und Jugendmedizin / Sektion für Neuropädiatrie & Stoffwechselmedizin, Heidelberg

75235

Children's Medical Center Dallas, Dallas

77030

University of Texas Health Science Center of Texas, Houston

80045

University of Colorado and the Children's Hospital CO, Aurora

84108

University of Utah, Division of Medical Genetics (pediatric and adult clinic), Salt Lake City

94304

Stanford University Center for Academic Medicine, Stanford

02115

Boston Children's Hospital, Boston

01009

Icahn School of Medicine at Mount Sinai (ISMMS), New York

SA 5000

PARC Clinical Research, Adelaide

90035-903

Hospital de clinicas de Porto Alegre, Porto Alegre

14051-140

Hospital das Clínicas da Faculdade de Medicina de Ribeirão Preto da Universidade de São Paulo, Ribeirão Preto

AB T2M 0L6

Metabolics and Genetics in Calgary (MAGIC) Clinic, Ltd., Calgary

M5G 1X8

The Hospital for Sick Children University of Toronto, Adult Clinic: The Fred A Litwin Family Centre in Genetic Medicine University Health Network & Mt. Sinai Hospital, Toronto

DK-2100

Copenhagen University Hospital, Rigshospitalet, Copenhagen

00185

Policlinico Umberto I, Rome

9713 GZ

UMCG Beatrix Children's Hospital, Groningen

4099-001

Centro Hospitalar Universitário Do Porto, Epe, Porto

1649-035

CENTRO HOSPITALAR UNIVERSITÁRIO LISBOA NORTE Hospital de Santa Maria,, Lisbon

CENTRO HOSPITALAR UNIVERSITÁRIO LISBOA NORTE Hospital de Santa Maria, Lisbon

B4 6DH

Birmingham Children's Hospital NHS Foundation Trust, Birmingham

WC1N 3JH

Great Ormond Street Hospital, London

Sponsors

Lead Sponsor

All Listed Sponsors
lead

PTC Therapeutics

INDUSTRY