Study Investigating NTLA-5001 in Subjects With Acute Myeloid Leukemia

PHASE1/PHASE2TerminatedINTERVENTIONAL
Enrollment

6

Participants

Timeline

Start Date

December 17, 2021

Primary Completion Date

July 21, 2022

Study Completion Date

August 31, 2022

Conditions
Acute Myeloid Leukemia
Interventions
GENETIC

Arm 1: NTLA-5001

"Autologous WT1-directed TCR T cells engineered ex vivo using CRISPR/Cas9 as intravenous infusion after pre-conditioning chemotherapy.~Cyclophosphamide and Fludarabine will be administered on Day -5, -4, and -3 as intravenous infusion."

GENETIC

Arm 2: NTLA-5001

"Autologous WT1-directed TCR T cells engineered ex vivo using CRISPR/Cas9 as intravenous infusion after pre-conditioning chemotherapy.~Cyclophosphamide and Fludarabine will be administered on Day -5, -4, and -3 as intravenous infusion."

Trial Locations (10)

33612

Research Site 5, Tampa

53226

Research Site 4, Milwaukee

77030

Research Site 3, Houston

90095

Research Site 2, Los Angeles

97239

Research Site 6, Portland

02114

Research Site 1, Boston

Unknown

Research Site 10, Leeds

Research Site 8, London

Research Site 9, London

Research Site 7, Manchester

Sponsors
All Listed Sponsors
lead

Intellia Therapeutics

INDUSTRY

NCT05066165 - Study Investigating NTLA-5001 in Subjects With Acute Myeloid Leukemia | Biotech Hunter | Biotech Hunter