48
Participants
Start Date
August 16, 2021
Primary Completion Date
March 31, 2029
Study Completion Date
March 31, 2039
ST-920
No study drug is administered in this study. Subjects who received ST-920 in a separate parent trial will be evaluated in this trial for long-term safety.
The Royal Melbourne Hospital, Parkville
Mt. Sinai Hospital, New York
Lysosomal & Rare Disorders Research & Treatment Center (LDRTC), Fairfax
Emory University School of Medicine, Atlanta
University of South Florida, Tampa
Cincinnati Children's Hospital Medical Center, Cincinnati
University of Iowa Hospital and Clinics, Iowa City
University of Minnesota Medical Center, Minneapolis
University of California, Irvine, Irvine
M.A.G.I.C. Clinic Ltd., Calgary
University Hospital of Würzburg, Würzburg
Royal Free Hospital, London
Addenbrooke's Hospital, Cambridge
Lead Sponsor
Sangamo Therapeutics
INDUSTRY