113
Participants
Start Date
December 1, 2021
Primary Completion Date
March 30, 2029
Study Completion Date
March 30, 2029
IPN60130
Immediate-release capsule containing high dose of the drug substance.
IPN60130
Immediate-release capsule containing low dose of the drug substance.
Placebo
Placebo will be supplied as powder filled hard capsules
Irccs Gaslini Institute, Genoa
The Children's Hospital of Philadelphia, Philadelphia
The Perelman School of Medicine - The University of Pennsylvania, Philadelphia
Hospital Universitario Ramon y Cajal, Pozuelo de Alarcón
Hospital Universitario Y Politecnico La Femerge, Valencia
Mayo Clinic, Rochester
Groupe Hospitalier Necker Enfants Malades, Paris
University of California San Francisco (UCSF), San Francisco
Hospital Italiano de Buenos Aires, Buenos Aires
Royal North Shore Hospital - New South Wales, Sydney
University Hospitals Leuven, Leuven
University of Alberta, Alberta Health Services (AHS), Edmonton
University Health Network (UHN), Toronto General Hospital (TGH), Toronto
Children's Hospital Capital Institute of Pediatrics (CIP), Beijing
Peking Union Medical College Hospital, Beijing
Shangai Children Medical Center, Shanghai
Tongi University - Tongi Hospital, Shanghai
Hopital Lariboisiere, Paris
Nagoya University Hospital, Nagoya
Aichi Children's Health and Medical Center, Ōbu
The University of Tokyo Hospital, Tokyo
Instituto Nacional De Rehabilitacion, Mexico City
Hospital Center Lisbon North, E.P.E- Hospital Santa Maria, Lisbon
Seoul National University Hospital, Seoul
Norrlands Universitetssjukhus, Umeå
Lead Sponsor
Collaborators (1)
Ipsen
INDUSTRY
Clementia Pharmaceuticals Inc.
INDUSTRY