An Open-Label Study of Oral NNZ-2591 in Pitt Hopkins Syndrome (PTHS-001)

PHASE2CompletedINTERVENTIONAL
Enrollment

28

Participants

Timeline

Start Date

October 14, 2022

Primary Completion Date

February 27, 2024

Study Completion Date

May 3, 2024

Conditions
Pitt Hopkins Syndrome
Interventions
DRUG

NNZ-2591

NNZ-2591 oral solution (50mg/mL) to be administered twice daily dose for 13 weeks.

Trial Locations (5)

35294

University of Alabama at Birmingham, Birmingham

60612

Rush University Medical Center, Chicago

75390

UT Southwestern, Dallas

80045

Children's Hospital Colorado, Aurora

94143

University of California at San Francisco, San Francisco

Sponsors
All Listed Sponsors
lead

Neuren Pharmaceuticals Limited

INDUSTRY

NCT05025332 - An Open-Label Study of Oral NNZ-2591 in Pitt Hopkins Syndrome (PTHS-001) | Biotech Hunter | Biotech Hunter