An Open-Label Study of Oral NNZ-2591 in Phelan-McDermid Syndrome (PMS-001)

PHASE2CompletedINTERVENTIONAL
Enrollment

18

Participants

Timeline

Start Date

August 8, 2022

Primary Completion Date

November 1, 2023

Study Completion Date

November 17, 2023

Conditions
Phelan-McDermid Syndrome
Interventions
DRUG

NNZ-2591

NNZ-2591 oral solution (50mg/mL) to be administered twice daily dose for 13 weeks.

Trial Locations (4)

60612

Rush University Medical Center, Chicago

77030

Texas Children's Hospital, Houston

02114

Massachusetts General Hospital, Boston

02115

Boston Children's Hospital, Boston

Sponsors
All Listed Sponsors
lead

Neuren Pharmaceuticals Limited

INDUSTRY

NCT05025241 - An Open-Label Study of Oral NNZ-2591 in Phelan-McDermid Syndrome (PMS-001) | Biotech Hunter | Biotech Hunter