A Retrospective Study of Subjects With Thymidine Kinase 2 Deficiency

CompletedOBSERVATIONAL
Enrollment

61

Participants

Timeline

Start Date

July 23, 2021

Primary Completion Date

January 21, 2022

Study Completion Date

January 21, 2022

Conditions
Thymidine Kinase 2 Deficiency
Interventions
OTHER

Observational retrospective data

Non-intervention

Trial Locations (12)

28041

Hospital Universitario 12 de Octubre, Madrid

34093

Istanbul Universitesi, Istanbul Tip Fakultesi, Fatih

34178

Yeditepe University Koşuyolu Hospital, Kadiköy

37916

East Tennessee Childrens Hospital, Knoxville

44308

Akron Children's Hospital, Akron

46202

Indiana University School of Medicine, Indianapolis

90095

David Geffen School of Medicine at UCLA, Los Angeles

125412

NIKI Pediatrii im Veltischeva, Children's Neuromuscular center, Moscow

394077

Medical Center Zdorovyy Rebenok, Voronezh

08035

Vall d'Hebron Institut de Recerca, Barcelona

08036

Hospital Clínic Barcelona, Barcelona

08041

Hospital de la Santa Creu i Sant Pau, Barcelona

All Listed Sponsors
lead

Zogenix MDS, Inc.

INDUSTRY

NCT05017818 - A Retrospective Study of Subjects With Thymidine Kinase 2 Deficiency | Biotech Hunter | Biotech Hunter