A Study Evaluating the Efficacy, Safety, Pharmacokinetics and Pharmacodynamics of Crovalimab in Pediatric Participants With Atypical Hemolytic Uremic Syndrome (aHUS)

PHASE3Active, not recruitingINTERVENTIONAL
Enrollment

41

Participants

Timeline

Start Date

November 17, 2021

Primary Completion Date

July 4, 2025

Study Completion Date

May 19, 2029

Conditions
Atypical Hemolytic Uremic Syndrome
Interventions
DRUG

Crovalimab

Crovalimab will be administered at a dose of 1000 mg intravenously (IV) (for participants weighing =\> 40 to \<100 kg) or 1500 mg IV (for participants weighing \>=100 kg) on Week 1 Day 1. On Week 1 Day 2 and on Weeks 2, 3 and 4, crovalimab will be administered at a dose of 340 mg subcutaneously (SC). On Week 5 and Q4W thereafter, it will be administered at a dose of 680 mg SC (for participants weighing =\> 40 to \<100 kg) or 1020 mg SC (for participants weighing \>=100 kg). Enrollment of participants weighing \<40 kg will be staggered using two weight-based dose confirmation groups (Group 1 participants weighing \>=20 kg to \<40 kg, followed by Group 2 participants weighing \>=5 kg to \<20 kg). All participants will receive an initial IV loading dose, which will be followed by SC dosing at either Q2W or Q4W intervals (depending on body weight), until study completion.

Trial Locations (22)

3000

UZ Leuven Gasthuisberg, Leuven

9000

UZ Gent, Ghent

34295

Hôpital Arnaud de Villeneuve, Montpellier

45116

Hospital de Especialidades Puerta de Hierro S.A de C.V., Zapopan

45229

Cincinnati Children's Hospital Medical Center, Cincinnati

68198

University of Nebraska, Omaha

75743

Gh Necker Enfants Malades, Paris

78229

UT Health Science Center, San Antonio

80045

Children's Hospital Colorado, Aurora

100034

Peking University First Hospital, Beijing

100045

Beijing Children's Hospital, Capital Medical University, Beijing

110029

All India Institute Of Medical Sciences (AIIMS), New Delhi

122001

Medanta-The Medicity, Gurgaon

310051

The children's hospital , Zhejiang university school of medicine, Hangzhou

380016

Institute of Kidney Diseases and Research Centre, Ahmedabad

07601

Hackensack University Medical Center, Hackensack

05403-900

Inst. Da Criança- Faculdade de Medicina Usp, São Paulo

H3T 1C5

CHU Sainte-Justine, Montreal

474-8710

Aichi Children?s Health and Medical Center, Aichi

266-0007

Chiba Children's Hospital, Chibashi, Chibaken

80-294

Uniwersyteckie Centrum Kliniczne, Gdansk

93-338

Instytut Centrum Zdrowia Matki Polki, Lodz

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

Chugai Pharmaceutical

INDUSTRY

lead

Hoffmann-La Roche

INDUSTRY

NCT04958265 - A Study Evaluating the Efficacy, Safety, Pharmacokinetics and Pharmacodynamics of Crovalimab in Pediatric Participants With Atypical Hemolytic Uremic Syndrome (aHUS) | Biotech Hunter | Biotech Hunter