Study to Assess the Safety, Tolerability, and Efficacy of Viltolarsen in Ambulant and Non-Ambulant Boys With DMD (Galactic53)

PHASE2CompletedINTERVENTIONAL
Enrollment

20

Participants

Timeline

Start Date

July 1, 2021

Primary Completion Date

June 20, 2023

Study Completion Date

July 13, 2023

Conditions
Duchenne Muscular Dystrophy
Interventions
DRUG

Viltolarsen

Received during weekly intravenous infusions

Trial Locations (8)

23219

Children's Hospital of Richmond at VCU, Richmond

34718

Yeditepe University Kosuyolu Hospital, Istanbul

117997

Russian National Research Medical University, Moscow

194100

Saint Petersburg State Paediatric Medical University, Saint Petersburg

410021

Hunan Children's Hospital, Changsha

1000053

The Third Medical Center of PLA General Hospital, Beijing

00168

Fondazione Policlinico Universitario A. Gemelli IRCCS - Universita Cattolica del Sacro Cuore, Roma

08950

Hospital Sant Joan de Deu, Barcelona

Sponsors

Lead Sponsor

Collaborators (1)

All Listed Sponsors
collaborator

Nippon Shinyaku Co., Ltd.

INDUSTRY

lead

NS Pharma, Inc.

INDUSTRY

NCT04956289 - Study to Assess the Safety, Tolerability, and Efficacy of Viltolarsen in Ambulant and Non-Ambulant Boys With DMD (Galactic53) | Biotech Hunter | Biotech Hunter