20
Participants
Start Date
July 1, 2021
Primary Completion Date
June 20, 2023
Study Completion Date
July 13, 2023
Viltolarsen
Received during weekly intravenous infusions
Children's Hospital of Richmond at VCU, Richmond
Yeditepe University Kosuyolu Hospital, Istanbul
Russian National Research Medical University, Moscow
Saint Petersburg State Paediatric Medical University, Saint Petersburg
Hunan Children's Hospital, Changsha
The Third Medical Center of PLA General Hospital, Beijing
Fondazione Policlinico Universitario A. Gemelli IRCCS - Universita Cattolica del Sacro Cuore, Roma
Hospital Sant Joan de Deu, Barcelona
Lead Sponsor
Collaborators (1)
Nippon Shinyaku Co., Ltd.
INDUSTRY
NS Pharma, Inc.
INDUSTRY