Efficacy and Safety of Ofatumumab and Siponimod Compared to Fingolimod in Pediatric Patients With Multiple Sclerosis

PHASE3Active, not recruitingINTERVENTIONAL
Enrollment

129

Participants

Timeline

Start Date

October 5, 2021

Primary Completion Date

March 2, 2027

Study Completion Date

November 19, 2031

Conditions
Multiple Sclerosis (MS)
Interventions
DRUG

Fingolimod

Fingolimod capsule administered orally once daily at a dose of either 0.5 mg or 0.25 mg (depending on patient's body weight).

DRUG

Ofatumumab

Ofatumumab as a solution for injection in an autoinjector containing 20 mg ofatumumab (50 mg/mL, 0.4 mL content) for subcutaneous administration. A loading dose at Day1, Day 7 and Day 14 and then injections every 4 weeks/ 6 weeks (depending on patient's body weight).

DRUG

Siponimod

Siponimod tablet administered orally once daily. Titration period, Day 1 to Day 6, first dose is either 0.1 mg or 0.25 mg up to daily dose of either 0.5 mg, 1 mg or 2 mg (depending on CYP2C9 genotype and body weight).

OTHER

Fingolimod placebo

Fingolimod matching placebo capsule

OTHER

Siponimod placebo

Siponimod matching placebo tablet

OTHER

Ofatumumab placebo

Ofatumumab matching placebo autoinjector

Trial Locations (51)

1090

Novartis Investigative Site, Vienna

3052

Novartis Investigative Site, Parkville

4130

Novartis Investigative Site, Esneux

9000

Novartis Investigative Site, Ghent

10000

Novartis Investigative Site, Zagreb

10002

Novartis Investigative Site, Taipei

11000

Novartis Investigative Site, Belgrade

11315

Novartis Investigative Site, Tallinn

20010

Childrens National Medical Center, Washington D.C.

33609

Axiom Clinical Research of Florida, Tampa

34090

Novartis Investigative Site, Montpellier

34098

Novartis Investigative Site, Istanbul

35575

Novartis Investigative Site, Izmir

37075

Novartis Investigative Site, Göttingen

41009

Novartis Investigative Site, Seville

41380

Novartis Investigative Site, Kocaeli

44791

Novartis Investigative Site, Bochum

48903

Novartis Investigative Site, Barakaldo

53226

Medical College of Wisconsin, Milwaukee

55200

Novartis Investigative Site, Samsun

67000

Novartis Investigative Site, Strasbourg

70403

Novartis Investigative Site, Tainan City

72202

Arkansas Childrens Hosp Rsch Inst, Little Rock

79106

Novartis Investigative Site, Freiburg im Breisgau

80131

Novartis Investigative Site, Napoli

90027

Childrens Hospital Los Angeles, Los Angeles

94275

Novartis Investigative Site, Le Kremlin-Bicêtre

226014

Novartis Investigative Site, Lucknow

700017

Novartis Investigative Site, Kolkata

4920235

Novartis Investigative Site, Petah Tikva

7691236

Novartis Investigative Site, Lo Barnechea

19104 4399

Childrens Hospital of Philadelphia, Philadelphia

C1181ACH

Novartis Investigative Site, CABA

81210-310

Novartis Investigative Site, Curitiba

90430-001

Novartis Investigative Site, Porto Alegre

05403-000

Novartis Investigative Site, São Paulo

H3A 2B4

Novartis Investigative Site, Montreal

H3T 1C5

Novartis Investigative Site, Montreal

01015

Novartis Investigative Site, Guatemala City

110 017

Novartis Investigative Site, New Delhi

00165

Novartis Investigative Site, Roma

LV-1004

Novartis Investigative Site, Riga

06700

Novartis Investigative Site, Mexico City

06720

Novartis Investigative Site, Mexico City

80-952

Novartis Investigative Site, Gdansk

93-338

Novartis Investigative Site, Lodz

60-355

Novartis Investigative Site, Poznan

04-730

Novartis Investigative Site, Warsaw

3000-602

Novartis Investigative Site, Coimbra

1169-050

Novartis Investigative Site, Lisbon

833 40

Novartis Investigative Site, Bratislava

Sponsors
All Listed Sponsors
lead

Novartis Pharmaceuticals

INDUSTRY