A Study of Pegcetacoplan in Pediatric Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

PHASE2RecruitingINTERVENTIONAL
Enrollment

12

Participants

Timeline

Start Date

February 4, 2021

Primary Completion Date

December 31, 2028

Study Completion Date

December 31, 2028

Conditions
Paroxysmal Nocturnal Hemoglobinuria (PNH)Paroxysmal Hemoglobinuria
Interventions
DRUG

Pegcetacoplan

Complement (C3) inhibitor

Trial Locations (12)

10400

RECRUITING

Phramongkutklao Hospital and College of Medicine, Bangkok

11000

RECRUITING

University Children's Hospital, Belgrade

30329

RECRUITING

Children's Hospital of Atlanta, Atlanta

50200

RECRUITING

Maharaj Nakorn Chiang Mai hospital, Chiang Mai

68000

RECRUITING

Hospital Ampang, Ampang

75009

NOT_YET_RECRUITING

Robert-Debré Hospital Paris, Paris

150 06

COMPLETED

Motol University Hospital, Prague

6525 GA

COMPLETED

Radboud University Hospital Nijmegen, Nijmegen

3508 GA

RECRUITING

University Medical Center Utrecht, Utrecht

E-08035

RECRUITING

University Hospital Vall d'Hebron, Barcelona

E-28041

RECRUITING

University Hospital 12 de Octubre, Madrid

W2 1NY

RECRUITING

St. Mary's Hospital, London

Sponsors
All Listed Sponsors
lead

Apellis Pharmaceuticals, Inc.

INDUSTRY

NCT04901936 - A Study of Pegcetacoplan in Pediatric Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) | Biotech Hunter | Biotech Hunter