A Study to Assess Safety, Pharmacokinetics, and Pharmacodynamics of mRNA-3705 in Participants With Isolated Methylmalonic Acidemia

PHASE1/PHASE2RecruitingINTERVENTIONAL
Enrollment

63

Participants

Timeline

Start Date

August 6, 2021

Primary Completion Date

August 1, 2026

Study Completion Date

August 1, 2028

Conditions
Methylmalonic Acidemia
Interventions
BIOLOGICAL

mRNA-3705

A sterile liquid for injection

Trial Locations (17)

2145

WITHDRAWN

Children's Hospital at Westmead, Westmead

3052

WITHDRAWN

Royal Children's Hospital Melbourne, Parkville

15706

RECRUITING

CHUS - H. Clinico U. de Santiago, Santiago de Compostela

19104

RECRUITING

The Children's Hospital of Philadelphia, Philadelphia

28041

RECRUITING

Hospital Universitario 12 de Octubre, Madrid

41013

RECRUITING

Hospital Universitario Virgen del Rocio - PPDS, Seville

48903

RECRUITING

Hospital Universitario Cruces, Barakaldo

75015

RECRUITING

Hôpital Necker - Enfants Malades, Paris

90095

RECRUITING

UCLA Medical Center, Los Angeles

94304

RECRUITING

Lucile Packard Children's Hospital at Stanford, Palo Alto

T6G 2R7

RECRUITING

Stollery Children's Hospital University of Alberta, Edmonton

M5G 1X8

RECRUITING

Hospital For Sick Children, Toronto

3015 AA

RECRUITING

Erasmus MC, Rotterdam

3584 CX

RECRUITING

Universitair Medisch Centrum Utrecht, Utrecht

08950

RECRUITING

Hospital Sant Joan de Deu - PIN, Esplugues de Llobregat

Unknown

TERMINATED

Birmingham Children's Hospital NHS Foundation Trust, Birmingham

M13 9WL

RECRUITING

Royal Manchester Childrens Hospital, Manchester

All Listed Sponsors
lead

ModernaTX, Inc.

INDUSTRY