Phase 3 Study to Evaluate Intravenous Trappsol(R) Cyclo(TM) in Pediatric and Adult Patients With Niemann-Pick Disease Type C1

UPMC Children's Hospital, Pittsburgh

Lysosomal and Rare Disorders Research & Treatment Center, Inc., Fairfax

Emory, Atlanta

University of Florida, Jacksonville

Cincinnati Children's Hospital Medical Center, Cincinnati

University Utah, Salt Lake City

UCSF Benioff Children's Hospital Oakland, Oakland

"Hospital de Alta Complejidad en Red El Cruce", Buenos Aires

Hospital de Niños de la Santísima Trinidad, Córdoba

Melbourne Children's Trials Centre Murdoch Children's Research Institute, Parkville

Royal Melbourne Hospital, Parkville

Metabolic Clinical Trials Unit, Adelaide

Hospital de Clínicas de Porto Alegre, Porto Alegre

Universidade de São Paulo, São Paulo

University of Campinas, São Paulo

SphinCS GmbH, Höchheim

University Munster, Münster

Emek Medical Center-Department of Pediatrics, Afula

Soroka Medical Center, Beersheba

University of Catania, Catania

Istituto Neurologico Carlo Besta, Milan

University Hospital of Padova, Padua

Centro di Coordinamento Regionale Malattie Rare, Udine

Szpital Uniwersytecki w Krakowie, Krakow

MediPark, Warsaw

King Faisal Specialist Hospital and Research Centre, Riyadh

Hospital Sant Joan de Déu - Neurology Department, Barcelona

Hospital Universitari de Bellvitge, Barcelona

Hospital Universitario 12 de Octubre, Madrid

National Taiwan University Hospital, Taipei

Gazi University Faculty of Medicine, Ankara

Ege University Medical School, Department of Inborn Errors of Metabolism, Izmir

Birmingham Children's Hospital NHS Foundation Trust · Department of Inherited Metabolic Disorders Service, Birmingham

University College London, London

Salford Royal Foundation NHS Trust, Salford