A Non-Interventional National Study in Pediatric Patients With Unexplained Enlarged Spleen

CompletedOBSERVATIONAL
Enrollment

60

Participants

Timeline

Start Date

June 30, 2021

Primary Completion Date

November 25, 2024

Study Completion Date

November 25, 2024

Conditions
Gaucher Disease, SplenomegalyAcid SphingoMyelinase Deficiency
Trial Locations (40)

13005

Investigational Site Number 2500005, Marseille

14033

Investigational Site Number 2500026, Caen

17000

Investigational Site Number 2500040, La Rochelle

21079

Investigational Site Number 2500006, Dijon

25030

Investigational Site Number 2500015, Besançon

29609

Investigational Site Number 2500038, Brest

30029

Investigational Site Number 2500022, Nîmes

33000

Investigational Site Number 2500003, Bordeaux

34090

Investigational Site Number 2500002, Montpellier

35203

Investigational Site Number 2500023, Rennes

38700

Investigational Site Number 2500007, La Tronche

42270

Investigational Site Number 2500017, Saint-Priest-en-Jarez

44000

Investigational Site Number 2500021, Nantes

49933

Investigational Site Number 2500014, Angers

51100

Investigational Site Number 2500029, Reims

54500

Investigational Site Number 2500012, Vandœuvre-lès-Nancy

59056

Investigational Site Number 2500037, Roubaix

59300

Investigational Site Number 2500025, Valenciennes

63000

Investigational Site Number 2500009, Clermont-Ferrand

64100

Investigational Site Number 2500039, Bayonne

66000

Investigational Site Number 2500013, Perpignan

67200

Investigational Site Number 2500004, Strasbourg

69008

Investigational Site Number 2500001, Lyon

69400

Investigational Site Number 2500010, Gleizé

73000

Investigational Site Number 2500018, Chambéry

75012

Investigational Site Number 2500016, Paris

76031

Investigational Site Number 2500024, Rouen

77100

Investigational Site Number 2500027, Meaux

77600

Investigational Site Number 2500031, Jossigny

78200

Investigational Site Number 2500032, Mantes-la-Jolie

78300

Investigational Site Number 2500035, Poissy

80054

Investigational Site Number 2500036, Amiens

86000

Investigational Site Number 2500011, Poitiers

87042

Investigational Site Number 2500030, Limoges

92700

Investigational Site Number 2500008, Colombes

94000

Investigational Site Number 2500028, Créteil

95107

Investigational Site Number 2500034, Argenteuil

06200

Investigational Site Number 2500019, Nice

Unknown

Investigational Site Number 2500033, Toulouse

Investigational Site Number 2500020, Tours

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Sanofi

INDUSTRY

NCT04845958 - A Non-Interventional National Study in Pediatric Patients With Unexplained Enlarged Spleen | Biotech Hunter | Biotech Hunter