22
Participants
Start Date
January 31, 2022
Primary Completion Date
February 28, 2032
Study Completion Date
February 28, 2032
No intervention
Access to any treatment is through authorized commercial use and not as part of this DMP
Johns Hopkins University, Baltimore
University of Virginia, Charlottesville
Vanderbilt University Medical Center, Nashville
Indiana University, Bloomington
Yale University, New Haven
IDIM - Instituto de Diagnóstico e Investigaciones Metabólicas, Buenos Aires
Ultragenyx Pharmaceutical Inc
INDUSTRY