A Study of Gene Therapy for Classic Congenital Adrenal Hyperplasia (CAH)

PHASE1/PHASE2Active, not recruitingINTERVENTIONAL
Enrollment

8

Participants

Timeline

Start Date

July 1, 2021

Primary Completion Date

February 28, 2029

Study Completion Date

February 28, 2029

Conditions
Congenital Adrenal Hyperplasia
Interventions
BIOLOGICAL

AAV BBP-631

intravenous

Trial Locations (5)

19104

Children's Hospital of Philadelphia, Philadelphia

28557

Lucas Research, Inc., Morehead City

55455

University of Minnesota, Minneapolis

60611

Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago

20892-1932

National Institutes of Health Clinical Center, Bethesda

Sponsors
All Listed Sponsors
lead

Adrenas Therapeutics Inc

INDUSTRY

NCT04783181 - A Study of Gene Therapy for Classic Congenital Adrenal Hyperplasia (CAH) | Biotech Hunter | Biotech Hunter