Cystic Fibrosis Transmembrane Regulator (CFTR) Biomarker Study to Evaluate the Rescue of Mutant CFTR in Patients With Cystic Fibrosis Treated With CFTR-modulators

RecruitingOBSERVATIONAL
Enrollment

200

Participants

Timeline

Start Date

July 1, 2018

Primary Completion Date

March 31, 2027

Study Completion Date

December 31, 2027

Conditions
Cystic Fibrosis
Interventions
DRUG

Treatment with cystic fibrosis transmembrane regulator (CFTR) modualtors Ivacaftor, Lumacaftor-Ivacaftor, Tezacaftor-Ivacaftor, Elexacaftor-Tezacaftor-Ivacaftor

observational

Trial Locations (4)

13353

RECRUITING

Charité - Universitätsmedizin Berlin, Berlin

Unknown

RECRUITING

Justus-Liebig-University Giessen, Giessen

RECRUITING

Hannover Medical School, Hanover

RECRUITING

University of Heidelberg, Heidelberg

All Listed Sponsors
collaborator

Hannover Medical School

OTHER

collaborator

Heidelberg University

OTHER

collaborator

University of Giessen

OTHER

lead

Charite University, Berlin, Germany

OTHER