NCT04724213View on ClinicalTrials.gov

Development of an Assessment Tool for Health-related Quality of Life in Children and Adolescents With Pompe Disease

NACompletedINTERVENTIONAL
Enrollment

101

Participants

Timeline

Start Date

July 1, 2021

Primary Completion Date

December 1, 2023

Study Completion Date

December 1, 2023

Conditions
Pompe Disease
Interventions
OTHER

Testing of reliability / validity of new questionnaire

Participants will answer new questionnaire and other, established, generic and chronic generic HrQol instruments

Trial Locations (1)

8032

University Childrens Hospital Zürich, Zurich

Sponsors

Collaborators (1)

Sanofi
All Listed Sponsors
collaborator

Sanofi

INDUSTRY

lead

University Children's Hospital, Zurich

OTHER