Study to Evaluate Safety, Pharmacokinetic and Pharmacodynamic Dose Escalation and Expansion Study of PXS-5505 in Patients With Primary, Post-polycythemia Vera or Post-essential Thrombocythemia Myelofibrosis

PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment

43

Participants

Timeline

Start Date

February 18, 2021

Primary Completion Date

July 9, 2025

Study Completion Date

July 9, 2025

Conditions
Myelofibrosis
Interventions
DRUG

PXS-5505

PXS-5505 is a hard capsule (size 0) with the additional excipients mannitol and magnesium stearate.

Trial Locations (23)

100

National Taiwan University Hospital - Hematology And Oncology, Taipei

613

Chang Gung Medical Foundation - ChiaYi Chang Gung Memorial Hospital - Hematology and Oncology, Chiayi City

807

Kaohsiung Medical University Chung-Ho Memorial Hospital, Kaohsiung City

2170

Liverpool Hospital, Liverpool

3065

St Vincent's Hospital Melbourne, Fitzroy

5037

Ashford Cancer Centre Research, Adelaide

6005

The Perth Blood Institute, West Perth

6009

One Clinical Research, Perth

10408

National Cancer Center (Seoul Metro; northern), Gyeonggi-do

13620

Seoul National University Hospital - Bundang, Gyeonggi-do

21565

Gachon University Gil Hospital, Incheon

27103

Novant Health Cancer Institute, Winston-Salem

40447

China Medical University Hospital - Internal Medicine - Taichung, Taichung

42601

Keimyung University Dongsan Hospital, Daegu

47392

Inje University Busan Paik Hospital - Internal Medicine, Busan

70403

National Cheng Kung University Hospital, Tainan City

77030

The University of Texas MD Anderson Cancer Center, Houston

98374

Comprehensive Cancer Center (UAB CCC), Birmingham

03080

Seoul National University Hospital, Seoul

03711

Severance Hospital, Yonsei University Health System- Haemat, Seoul

05505

Asan Medical Centre, Seoul

06351

Samsung Medical Center, Seoul

06591

The Catholic University of Korea, Seoul St. Mary's Hospital, Seoul

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Syntara

INDUSTRY