Long-Chain Fatty Acid Oxidation Disorders In-Clinic Disease Monitoring Program

RecruitingOBSERVATIONAL
Enrollment

150

Participants

Timeline

Start Date

November 30, 2021

Primary Completion Date

December 31, 2035

Study Completion Date

December 31, 2035

Conditions
Long-chain Fatty Acid Oxidation Disorders (LC-FAOD)
Interventions
OTHER

No Intervention

No Intervention

Trial Locations (16)

10032

RECRUITING

Columbia University, New York

15224

RECRUITING

Children's Hospital of Pittsburgh of UPMC, Pittsburgh

30322

RECRUITING

The Emory Clinic, Atlanta

33606

RECRUITING

University of South Florida, Tampa

43205

RECRUITING

Nationwide Children's Hospital, Columbus

55454

RECRUITING

University of Minnesota, Minneapolis

60611

RECRUITING

Ann & Robert H. Lurie Children's Hospital, Chicago

80045

RECRUITING

Children's Hospital of Colorado, Aurora

84108

RECRUITING

University of Utah, Salt Lake City

85016

RECRUITING

Phoenix Children's Hospital, Phoenix

94158

RECRUITING

University of California San Francisco, San Francisco

98020

RECRUITING

Seattle Children's Hospital, Seattle

02215

RECRUITING

Boston Children's Hospital, Boston

T6G 1C9

RECRUITING

University of Alberta, Edmonton

K1H 8L1

RECRUITING

CHEO (Children's Hospital Eastern Ontario), Ottawa

M5G 1X8

RECRUITING

SickKids (The Hospital for Sick Children), Toronto

All Listed Sponsors
lead

Ultragenyx Pharmaceutical Inc

INDUSTRY