French Prospective, Observational Cohort Study of Patients With Fabry Disease Treated With Migalastat

CompletedOBSERVATIONAL
Enrollment

48

Participants

Timeline

Start Date

October 15, 2020

Primary Completion Date

June 30, 2023

Study Completion Date

June 30, 2023

Conditions
Fabry Disease
Interventions
OTHER

Noninterventional

Not applicable; Noninterventional study

Trial Locations (13)

Unknown

CHU Angers, Angers

CHU de Bordeaux, Bordeaux

Hôpital Pellegrin, Bordeaux

CHU Caen, Caen

CHU Lille, Lille

Hôpital femme mère enfant, Lyon

"Hôpital de la Conception , AP-HM"

CHU de Nancy, Nancy

CHU Nantes Hôtel Dieu, Nantes

Hôpital de la Croix Saint Simon, Paris

Hôpital Tenon AP-HP, Paris

Hôpitaux Universitaires de Strasbourg, Strasbourg

CHU Toulouse Rangueil, Toulouse

Sponsors
All Listed Sponsors
lead

Amicus Therapeutics France SAS

INDUSTRY

NCT04602364 - French Prospective, Observational Cohort Study of Patients With Fabry Disease Treated With Migalastat | Biotech Hunter | Biotech Hunter