NCT04581785View on ClinicalTrials.gov

Gene Therapy With hLB-001 in Pediatric Patients With Severe Methylmalonic Acidemia

PHASE1/PHASE2TerminatedINTERVENTIONAL
Enrollment

4

Participants

Timeline

Start Date

May 29, 2021

Primary Completion Date

January 10, 2023

Study Completion Date

January 10, 2023

Conditions
Methylmalonic Acidemia
Interventions
BIOLOGICAL

hLB-001

hLB-001 via IV infusion

Trial Locations (4)

15224

Clinical Trial Site, Pittsburgh

30322

Clinical Trial Site, Atlanta

37232

Clinical Trial Site, Nashville

98105

Clinical Trial Site, Seattle

Sponsors
All Listed Sponsors
collaborator

Alexion Pharmaceuticals, Inc.

INDUSTRY

lead

LogicBio Therapeutics, Inc

INDUSTRY